Summer is half over, so I thought I’d update a few posts. EMAN IN LIBERIA A year ago, I frantically wrote about my young friend in Liberia, Emmanuel Gokpolu, and his pleas to help stop Ebola.
During Rare Disease Week, I turn over DNA Science to a family battling a rare inherited disease. I’ve been following Max Randell, who has Canavan disease, in my human genetics textbook since he was a preschooler
As enthusiasm for dumping ice on one another fades with autumn and October brings pervasive pink, I wish that attention would turn to families confronting diseases not as well known as ALS and breast cancer.
If ten science writers were asked to write a book about gene therapy, a biotechnology with roots going back to the 1950s, they could tell ten different stories. VARIATIONS ON THE THEME Any account of
Gene therapy has been in the news recently, for awards. The same day that publisher Mary Ann Liebert Inc. honored 12 “pioneers in gene therapy,” one of the youngest patients, 13-year-old Corey Haas, won school-wide
I’m thrilled about the encouraging gene therapy results just published in Science Translational Medicine from Paola Leone, PhD and Jude Samulski, PhD, colleagues. “Long-term follow-up after gene therapy for Canavan Disease” updates a project that has its