Blog Archives

Gene Therapy for Blindness Works!

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AGTC Tackles 3 Eye Diseases with Gene Therapy

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Fighting Canavan: Honoring Rare Disease Week

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SCID-X1 Gene Therapy, Take 2

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Catching Up With 3 Rare Disease Families

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Eliza’s Journey: Part 2

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Eliza’s Journey: Part 1

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A Checklist for Gene Therapy From the UK Cystic Fibrosis Trial

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Rare Disease Day 2014: A Parent Fights to Cure Blindness

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Gene Therapy News: Brain, Skin, Eye

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